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EP3806868A4 - EXON-SKIPPING OLIGOMERS FOR MUSCULAR DYSTROPHY - Google Patents

EXON-SKIPPING OLIGOMERS FOR MUSCULAR DYSTROPHY
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Publication number
EP3806868A4
EP3806868A4EP19818767.6AEP19818767AEP3806868A4EP 3806868 A4EP3806868 A4EP 3806868A4EP 19818767 AEP19818767 AEP 19818767AEP 3806868 A4EP3806868 A4EP 3806868A4
Authority
EP
European Patent Office
Prior art keywords
exon
muscular dystrophy
skipping
oligomers
skipping oligomers
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Withdrawn
Application number
EP19818767.6A
Other languages
German (de)
French (fr)
Other versions
EP3806868A2 (en
Inventor
Frederick Joseph SCHNELL
Marco Passini
Neisa ESTRELLA
Gunnar Hanson
Ming Zhou
Richard Bestwick
Current Assignee (The listed assignees may be inaccurate. Google has not performed a legal analysis and makes no representation or warranty as to the accuracy of the list.)
Sarepta Therapeutics Inc
Original Assignee
Sarepta Therapeutics Inc
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Sarepta Therapeutics IncfiledCriticalSarepta Therapeutics Inc
Priority to EP22214630.0ApriorityCriticalpatent/EP4219717A3/en
Priority claimed from PCT/US2019/036764external-prioritypatent/WO2019241385A2/en
Publication of EP3806868A2publicationCriticalpatent/EP3806868A2/en
Publication of EP3806868A4publicationCriticalpatent/EP3806868A4/en
Withdrawnlegal-statusCriticalCurrent

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EP19818767.6A2018-06-132019-06-12 EXON-SKIPPING OLIGOMERS FOR MUSCULAR DYSTROPHYWithdrawnEP3806868A4 (en)

Priority Applications (1)

Application NumberPriority DateFiling DateTitle
EP22214630.0AEP4219717A3 (en)2018-06-132019-06-12Exon skipping oligomers for muscular dystrophy

Applications Claiming Priority (2)

Application NumberPriority DateFiling DateTitle
US201862684615P2018-06-132018-06-13
PCT/US2019/036764WO2019241385A2 (en)2018-06-132019-06-12Exon skipping oligomers for muscular dystropy

Related Child Applications (1)

Application NumberTitlePriority DateFiling Date
EP22214630.0ADivisionEP4219717A3 (en)2018-06-132019-06-12Exon skipping oligomers for muscular dystrophy

Publications (2)

Publication NumberPublication Date
EP3806868A2 EP3806868A2 (en)2021-04-21
EP3806868A4true EP3806868A4 (en)2022-06-22

Family

ID=74879743

Family Applications (2)

Application NumberTitlePriority DateFiling Date
EP19818767.6AWithdrawnEP3806868A4 (en)2018-06-132019-06-12 EXON-SKIPPING OLIGOMERS FOR MUSCULAR DYSTROPHY
EP22214630.0APendingEP4219717A3 (en)2018-06-132019-06-12Exon skipping oligomers for muscular dystrophy

Family Applications After (1)

Application NumberTitlePriority DateFiling Date
EP22214630.0APendingEP4219717A3 (en)2018-06-132019-06-12Exon skipping oligomers for muscular dystrophy

Country Status (1)

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EP (2)EP3806868A4 (en)

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US20120289457A1 (en)*2011-05-052012-11-15Avi Biopharma, Inc.Peptide oligonucleotide conjugates
WO2017062835A2 (en)*2015-10-092017-04-13Sarepta Therapeutics, Inc.Compositions and methods for treating duchenne muscular dystrophy and related disorders

Non-Patent Citations (2)

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Title
CHARLESTON JAY S. ET AL: "Eteplirsen treatment for Duchenne muscular dystrophy : Exon skipping and dystrophin production", NEUROLOGY, vol. 90, no. 24, 12 June 2018 (2018-06-12), US, pages e2146 - e2154, XP055877433, ISSN: 0028-3878, Retrieved from the Internet <URL:https://n.neurology.org/content/neurology/90/24/e2146.full.pdf> DOI: 10.1212/WNL.0000000000005680*
GOEMANS NATHALIE ET AL: "A randomized placebo-controlled phase 3 trial of an antisense oligonucleotide, drisapersen, in Duchenne muscular dystrophy", NEUROMUSCULAR DISORDERS, vol. 28, no. 1, 1 January 2018 (2018-01-01), GB, pages 4 - 15, XP055877283, ISSN: 0960-8966, DOI: 10.1016/j.nmd.2017.10.004*

Also Published As

Publication numberPublication date
EP4219717A3 (en)2023-12-20
EP3806868A2 (en)2021-04-21
EP4219717A2 (en)2023-08-02

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